Outcome of haematopoietic cell transplantation in children with lysosomal acid lipase deficiency: a study on behalf of the EBMT Inborn Errors Working Party

Lum, Su Han; Minkov, Milen; Jones, Simon A.; Hazelaar, Sheree; Sirait, Tiarlan; Potter, Jane E.; Stepensky, Polina; Garban, Frederic; Pichler, Herbert; Stein, Jerry; Kaya, Zuhre; Schulz, Ansgar; Mellgren, Karin; Diaz de Heredia, Cristina; Pochon, Cecile; Riesco, Susana; Diaz, Miguel Angel; Michel, Gérard; Lindemans, Caroline; Gruhn, Bernd; Albert, Michael H.; Lankester, Arjan C.; Neven, Bénédicte; Wynn, Robert