Clinically meaningful improvements in patient-reported outcomes in mitapivat-treated patients with pyruvate kinase deficiency

Kuo, Kevin H.M.; Grace, Rachael F.; van Beers, Eduard J.; Barcellini, Wilma; Glenthøj, Andreas; Holzhauer, Susanne; Beynon, Vanessa; Morris, Susan; Li, Junlong; Zagadailov, Erin; Patel, Parija; Al-Samkari, Hanny

doi:https://doi.org/10.1002/ajh.27312

Clinically meaningful improvements in patient-reported outcomes in mitapivat-treated patients with pyruvate kinase deficiency

DSpace/Manakin Repository

Clinically meaningful improvements in patient-reported outcomes in mitapivat-treated patients with pyruvate kinase deficiency

Kuo, Kevin H.M.; Grace, Rachael F.; van Beers, Eduard J.; Barcellini, Wilma; Glenthøj, Andreas; Holzhauer, Susanne; Beynon, Vanessa; Morris, Susan; Li, Junlong; Zagadailov, Erin; Patel, Parija; Al-Samkari, Hanny

(2024) American journal of hematology, volume 99, issue 7, pp. 1415 - 1419

(Letter)

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Keywords: Hematology

DOI: https://doi.org/10.1002/ajh.27312

ISSN: 0361-8609

Publisher: John Wiley & Sons Inc.

(Peer reviewed)