Novel treatment options to improve aberrant pre-messenger RNA splicing and protein folding in ATP8B1 deficiency
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Novel treatment options to improve aberrant pre-messenger RNA splicing and protein folding in ATP8B1 deficiency
van der Woerd, WL; Mulder, Johanna; Pagani, Franco; Beuers, Ulrich; Houwen, RHJ; van de Graaf, Stan F. J.
(2015) Journal of Hepatology, pp.
(Abstract)
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ISSN: 0168-8278
Publisher: Elsevier