Cost-effectiveness analysis and prevention effects of ultra-orphan drugs for rare diseases: An in silico model applied to Cryopyrin Associated Periodic Syndromes (CAPS)
DSpace/Manakin Repository
Cost-effectiveness analysis and prevention effects of ultra-orphan drugs for rare diseases: An in silico model applied to Cryopyrin Associated Periodic Syndromes (CAPS)
Trieste, L.; Della Casa Alberighi, O.; Turchetti, G.; Pierotti, F.; Accame, L.; Lorenzoni, V.; Frenkel, J.; Gattorno, M.; Quartier, P.; Martini, A.